ARTEMIS (DCLRE1C ) DEFICIENT SEVERE COMBINED IMMUNODEFICIENCY

Clinical trials for ARTEMIS (DCLRE1C ) DEFICIENT SEVERE COMBINED IMMUNODEFICIENCY explained in plain language.

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Trials to join now! 1

One-Time gene therapy aims to cure 'Bubble Boy' disease

⭐️ CURE ⭐️ Recruiting now

This early-stage trial is testing a one-time gene therapy for babies with a rare and severe form of immune deficiency called Artemis SCID. Doctors take a patient's own blood stem cells, use a virus to insert a corrected gene in the lab, and then transplant the cells back. The goa…

Matched conditions: ARTEMIS (DCLRE1C ) DEFICIENT SEVERE COMBINED IMMUNODEFICIENCY

Phase: PHASE1, PHASE2 • Sponsor: Assistance Publique - Hôpitaux de Paris • Aim: ⭐️ CURE ⭐️

Last updated Mar 31, 2026 12:12 UTC

ARTEMIS (DCLRE1C ) DEFICIENT SEVERE COMBINED IMMUNODEFICIENCY

Get alerted when new ARTEMIS (DCLRE1C ) DEFICIENT SEVERE COMBINED IMMUNODEFICIENCY trials appear

One-Time gene therapy aims to cure 'Bubble Boy' disease