ANGELMAN SYNDROME

Clinical trials for ANGELMAN SYNDROME explained in plain language.

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Trials to join now! 7 Not yet recruiting 1 Not yet finished but already full! 4 Completed 3

New hope for angelman syndrome: drug trial targets brain function

Disease control Not yet recruiting

This study tests a drug called rugonersen, given via spinal injection, to see if it can improve thinking and communication skills in people with Angelman syndrome. The trial includes 165 children and adults aged 1 to 50. Researchers will compare the drug against a sham procedure …

Matched conditions: ANGELMAN SYNDROME

Phase: PHASE3 • Sponsor: OHB Pediatrics Ltd. • Aim: Disease control

Last updated Jun 27, 2026 13:03 UTC

ANGELMAN SYNDROME

Get alerted when new ANGELMAN SYNDROME trials appear

New hope for angelman syndrome: drug trial targets brain function