ANEMIA, HEMOLYTIC

Clinical trials for ANEMIA, HEMOLYTIC explained in plain language.

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Not yet finished but already full! 1

Lifeline drug mitapivat keeps flowing for rare blood disorder patients

Disease control ENROLLING_BY_INVITATION

This study offers continued access to the drug mitapivat for adults with pyruvate kinase deficiency who completed an earlier Agios-sponsored trial and cannot get the drug commercially. Only 6 participants are enrolled, and the main goal is to monitor side effects. The study does …

Matched conditions: ANEMIA, HEMOLYTIC

Phase: PHASE4 • Sponsor: Agios Pharmaceuticals, Inc. • Aim: Disease control

Last updated Jun 27, 2026 14:03 UTC

ANEMIA, HEMOLYTIC

Get alerted when new ANEMIA, HEMOLYTIC trials appear

Lifeline drug mitapivat keeps flowing for rare blood disorder patients