ANEMIA, HEMOLYTIC

Clinical trials for ANEMIA, HEMOLYTIC explained in plain language.

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Not yet finished but already full! 1

Lifeline extended: patients get continued access to rare disease drug

Disease control ENROLLING_BY_INVITATION

This study provides continued access to the drug mitapivat for people with pyruvate kinase deficiency who completed earlier research studies. It's for participants who benefited from the drug but can't get it through regular commercial channels. The main goal is to monitor safety…

Matched conditions: ANEMIA, HEMOLYTIC

Phase: PHASE4 • Sponsor: Agios Pharmaceuticals, Inc. • Aim: Disease control

Last updated Mar 20, 2026 14:48 UTC

ANEMIA, HEMOLYTIC

Get alerted when new ANEMIA, HEMOLYTIC trials appear

Lifeline extended: patients get continued access to rare disease drug