ALEXANDER DISEASE

Clinical trials for ALEXANDER DISEASE explained in plain language.

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Trials to join now! 2 Not yet finished but already full! 1 Completed 1

Experimental drug offers hope for rare brain disorder

Disease control Ongoing

This study is testing whether a new drug called ION373 can help improve or stabilize movement and motor function in people with Alexander disease, a rare genetic brain disorder. About 54 patients aged 2-65 will receive either the drug or a placebo for 60 weeks, followed by the dr…

Matched conditions: ALEXANDER DISEASE

Phase: PHASE3 • Sponsor: Ionis Pharmaceuticals, Inc. • Aim: Disease control

Last updated Apr 01, 2026 14:42 UTC

ALEXANDER DISEASE

Get alerted when new ALEXANDER DISEASE trials appear

Experimental drug offers hope for rare brain disorder