ALEXANDER DISEASE

Clinical trials for ALEXANDER DISEASE explained in plain language.

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Trials to join now! 3 Not yet finished but already full! 1 Completed 1

Experimental drug zilganersen aims to slow rare brain disease

Disease control Ongoing

This Phase 3 trial tests whether zilganersen (ION373) can improve or stabilize motor function in people with Alexander disease, a rare genetic brain disorder. Fifty-four participants aged 2 to 65 will receive either the drug or a placebo injected into the spine. The study measure…

Matched conditions: ALEXANDER DISEASE

Phase: PHASE3 • Sponsor: Ionis Pharmaceuticals, Inc. • Aim: Disease control

Last updated Jun 27, 2026 12:03 UTC

ALEXANDER DISEASE

Get alerted when new ALEXANDER DISEASE trials appear

Experimental drug zilganersen aims to slow rare brain disease