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Retinal ciliopathy

MONDO:0022410

15 clinical trials for this condition and its sub-types.

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Sub-types

Leber congenital amaurosis 10 (2) Cone-rod dystrophy 16 (0) Leber congenital amaurosis with early-onset deafness (0) Retinitis pigmentosa 23 (0) Retinitis pigmentosa 51 (0) Retinitis pigmentosa 55 (0) Retinitis pigmentosa 64 (0) Retinitis pigmentosa 74 (0) Retinitis pigmentosa 80 (0)

Broader categories

Disease (717) Nervous system disorder (243) Hereditary disease (188) Eye disorder (104) Retinal disorder (89) Human disease (15) Hereditary neurological disease (6) Disorder of orbital region (3) Ciliopathy (2) Disease by molecular mechanism (2)

Trials to join now! 6 Not yet recruiting 1 Not yet finished but already full! 1 Completed 6 Terminated 1

Can a single eye injection restore sight in genetic blindness?

Cure Ongoing

This trial tests an experimental gene therapy called OCU400 in people with retinitis pigmentosa or Leber congenital amaurosis, which are inherited conditions that cause progressive vision loss and can lead to blindness. The therapy is given as a single injection into the eye, wit…

Phase 1/2 • Sponsor: Ocugen • Aim: Cure

Last updated Aug 02, 2026 00:00 UTC