Paroxysmal nocturnal hemoglobinuria 2
MONDO:0014166Any paroxysmal nocturnal hemoglobinuria in which the cause of the disease is a mutation in the PIGT gene.
Also known as: PIGT paroxysmal nocturnal hemoglobinuria, paroxysmal nocturnal hemoglobinuria 2, paroxysmal nocturnal hemoglobinuria 2, autosomal dominant, somatic mutation, paroxysmal nocturnal hemoglobinuria caused by mutation in PIGT, paroxysmal nocturnal hemoglobinuria type 2, PNH2
62 clinical trials for this condition and its sub-types.
Follow this condition — get notified about new trials