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GBA1-related Parkinson disease, susceptibility

MONDO:1040030

A susceptibility or predisposition to Parkinsons disease in which the cause of the disease is the presence of a monoallelic pathogenic variant or risk allele in the GBA1 gene.

6 clinical trials for this condition and its sub-types, 6 tagged with GBA1-related Parkinson disease, susceptibility itself.

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↑ Inherited disease susceptibility (1315)

Including sub-types (6) Tagged with GBA1-related Parkinson disease, susceptibility (6)

Trials to join now! 1 Not yet recruiting 2 Not yet finished but already full! 3

Cough medicine repurposed: ambroxol registry launches for rare brain diseases

Knowledge-focused Recruiting now

This study creates a registry to collect real-world information on the safety and effectiveness of ambroxol, a common cough medicine, when used at higher doses for Gaucher disease or GBA-related Parkinson disease. Researchers aim to gather data from 300 patients worldwide who are…

Sponsor: Shaare Zedek Medical Center • Aim: Knowledge-focused

Last updated Jun 27, 2026 12:24 UTC