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DNM1-encephalopathy and neurodevelopmental disorder

MONDO:0700339

A developmental and epileptic encephalopathy in which the cause of the disease is a variation in the DNM1 gene.

Also known as: DNM1-related DEE, DNM1-related developmental and epileptic encephalopathy

17 clinical trials for this condition and its sub-types, 0 tagged with DNM1-encephalopathy and neurodevelopmental disorder itself.

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Where it sits in the disease tree

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Part of

↑ Genetic developmental and epileptic encephalopathy (83)

Sub-types of DNM1-encephalopathy and neurodevelopmental disorder

Developmental and epileptic encephalopathy, 31A 0 trials
Developmental and epileptic encephalopathy, 31B 0 trials

Including sub-types (17) Tagged with DNM1-encephalopathy and neurodevelopmental disorder (0)

Trials to join now! 5 Not yet finished but already full! 6 Completed 5 Terminated 1

New drug shows promise for Tough-to-Treat seizures in kids

Disease control Stopped early

This study looked at the long-term safety of soticlestat, an experimental drug, in children and adults with severe forms of epilepsy like Dravet syndrome and Lennox-Gastaut syndrome. Participants took soticlestat twice a day along with their usual seizure medicines. The study was…

Phase 2 • Sponsor: Takeda • Aim: Disease control

Last updated Sep 06, 2026 00:00 UTC