New hope for kids with rare bleeding disorder: drug aims to stop bleeds before they start
NCT ID NCT05582993
First seen Nov 01, 2025
Summary
This study tests a drug called vonicog alfa to prevent bleeding in 24 children with severe von Willebrand disease, a condition that causes easy bruising and heavy bleeding. Participants receive the drug regularly for 12 months to see if it reduces bleeding episodes compared to their past experiences. The goal is to improve daily life by controlling the disease with ongoing treatment.
Disclaimer
Read more
Show less
This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for VON WILLEBRAND DISEASE (VWD) are added.
By submitting, you agree to our Terms of use
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
By submitting, you agree to our Terms of use
Study contacts
-
Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
-
Azienda Ospedaliera Pediatrica Santobono Pausillipon
ACTIVE_NOT_RECRUITINGNaples, 80123, Italy
-
Azienda Ospedaliero-Universitaria Città della Salute e della Scienza di Torino
ACTIVE_NOT_RECRUITINGTurin (Torino), 10126, Italy
-
Bleeding and Clotting Disorders Institute
RECRUITINGPeoria, Illinois, 61614, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
Children's Health Care d/b/a Children's Minnesota
RECRUITINGMinneapolis, Minnesota, 55404, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
-
Children's Health Ireland
RECRUITINGDublin, D12N512, Ireland
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
Childrens Hospital of Michigan
RECRUITINGDetroit, Michigan, 48201, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
Cure 4 the Kids
RECRUITINGLas Vegas, Nevada, 89135, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
Haemophilia Comprehensive Care Centre, Great Ormond Street Hospital for Children NHS Foundation Trust
RECRUITINGLondon, WC1N 3HR, United Kingdom
Contact
Contact Email: •••••@•••••
-
Hemostase Clinique - Institut Cœur-Poumons (4eme étage aile est) Bureau 419
RECRUITINGLille, 59037, France
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
-
Hopital Edouard Herriot - CHU Lyon
RECRUITINGLyon, 69677, France
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
Japanese Red Cross Narita Hospital
RECRUITINGNarita, Chiba, 286-8523, Japan
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
-
Medical University of South Carolina (MUSC)
RECRUITINGCharleston, South Carolina, 29425, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
Michigan State University Center for Bleeding Disorders & Clotting Disorders
RECRUITINGEast Lansing, Michigan, 48824, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
NHO Beppu Medical Center
RECRUITINGBeppu, Oita Prefecture, 874-0011, Japan
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
Nagasaki University Hospital
RECRUITINGNagasaki, 852-8501, Japan
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
-
Nara Medical University Hospital
RECRUITINGKashihara, Nara, 634-8522, Japan
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
New York - Presbyterian/Weill Cornell Medical Center
RECRUITINGNew York, New York, 10021, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
Riley Hospital for Children Indiana University Health
RECRUITINGIndianapolis, Indiana, 46202, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
Rutgers - Robert Wood Johnson Medical School
RECRUITINGNew Brunswick, New Jersey, 08901, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
-
University of Alabama at Birmingham
RECRUITINGBirmingham, Alabama, 35223, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
University of Iowa Hospitals & Clinics PARENT
RECRUITINGIowa City, Iowa, 52242, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.