New drug hope for kids with rare Muscle-Weakening disease

NCT ID NCT06149559

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study tests a drug called rozanolixizumab in 12 children aged 2 to 18 with moderate to severe generalized myasthenia gravis, a condition that causes muscle weakness. The goal is to see if the drug is safe and helps control symptoms. Participants receive injections, and researchers monitor side effects and changes in antibody levels.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for GENERALIZED MYASTHENIA GRAVIS are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Locations

  • Mg0006 20081

    Taipei, Taiwan

  • Mg0006 20095

    Taipei, Taiwan

  • Mg0006 20339

    Ōbu, Japan

  • Mg0006 20340

    Fuchu-shi, Japan

  • Mg0006 20343

    Sagamihara, Japan

  • Mg0006 40144

    Milan, Italy

  • Mg0006 40155

    Warsaw, Poland

  • Mg0006 40290

    Bologna, Italy

  • Mg0006 40733

    Naples, Italy

  • Mg0006 40734

    Warsaw, Poland

  • Mg0006 40836

    Kocaeli, Turkey (Türkiye)

  • Mg0006 40841

    Altindağ/ankara, Turkey (Türkiye)

  • Mg0006 40843

    Ankara, Turkey (Türkiye)

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

rozanolixizumab

What this could lead to

If it works, this could provide a new treatment option for children with generalized myasthenia gravis, helping control muscle weakness and improve daily life.

What could go wrong

This is a small, early-phase study with only 12 participants, so results may not apply to all children. The drug may cause serious side effects like infections or headaches.

Conditions

The condition(s) this trial relates to.

myasthenia gravis

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.