New hope for rare brain disease: expanded access program opens
NCT ID NCT07487389
First seen Apr 11, 2026 · Last updated May 20, 2026 · Updated 5 times
Summary
This program offers zilganersen to people with Alexander disease, a rare genetic condition that damages the nervous system. It is for US residents aged 2 and older who have not responded to or cannot tolerate other treatments. The goal is to provide access to this experimental drug while more research continues.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Genom att skicka in godkänner du våra Användarvillkor
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Genom att skicka in godkänner du våra Användarvillkor
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Conditions
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