Scientists track rare muscle Disease's natural course
NCT ID NCT04823143
First seen Apr 04, 2026 · Last updated May 21, 2026 · Updated 8 times
Summary
This study followed 44 adults with a confirmed VCP gene mutation to learn how their disease (IBMPFD) naturally progresses over one year. Participants completed walking tests, strength assessments, and questionnaires about daily function and quality of life. The goal was to gather data to help design future treatment trials, not to test any therapy.
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the original study
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
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Genom att skicka in godkänner du våra Användarvillkor
Locations
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Nationwide Children's Hospital
Columbus, Ohio, 43205, United States
Conditions
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