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Gene therapy trial targets genetic heart disease

NCT ID NCT05836259

First seen Mar 24, 2026 · Last updated May 23, 2026 · Updated 6 times

Summary

This study tests a new gene therapy, TN-201, in 30 adults with a type of heart muscle disease caused by a specific gene mutation (MYBPC3). The goal is to see if it is safe and can improve heart function and symptoms. Participants receive a single dose and are followed for side effects and quality of life changes.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Brigham and Women's Hospital

    WITHDRAWN

    Boston, Massachusetts, 02115, United States

  • Cleveland Clinic

    RECRUITING

    Cleveland, Ohio, 44195, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Emory University

    WITHDRAWN

    Atlanta, Georgia, 30322, United States

  • Hospital of the University of Pennsylvania

    WITHDRAWN

    Philadelphia, Pennsylvania, 19104, United States

  • Houston Methodist Hospital

    RECRUITING

    Houston, Texas, 77030, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Mayo Clinic

    RECRUITING

    Rochester, Minnesota, 55905, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Oregon Health & Science University

    WITHDRAWN

    Portland, Oregon, 97239, United States

  • The Christ Hospital Physicians - The Ohio Heart and Vascular Center

    WITHDRAWN

    Cincinnati, Ohio, 45219, United States

  • UC San Diego Altman Clinical and Translational Research Institute - Center for Clinical Research

    RECRUITING

    La Jolla, California, 92093, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University of California San Francisco

    RECRUITING

    San Francisco, California, 94117, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.