New drug shows promise for rare nerve disorder that steals mobility
NCT ID NCT05397665
First seen Nov 01, 2025 · Last updated May 23, 2026 · Updated 23 times
Summary
This study tests an experimental drug called AT-007 in adults with a rare inherited nerve disease (SORD deficiency) that causes weakness and trouble walking. The drug aims to lower harmful sorbitol levels in the body and improve walking speed over 24 months. About 56 participants will receive either AT-007 or a placebo in a double-blind design.
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This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Axon Clinical, s.r.o.
Prague, Prague, 150 00, Czechia
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Fondazione IRCCS Istituto Neurologico "Carlo Besta"
Milan, Milano, 20133, Italy
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Hassman Research Institute
Berlin, New Jersey, 08009, United States
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Massachusetts General Hospital
Boston, Massachusetts, 02114, United States
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University College of London
London, London, WC1E 6BT, United Kingdom
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University of Colorado
Aurora, Colorado, 80045, United States
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University of Iowa
Iowa City, Iowa, 52242, United States
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University of Miami
Coral Gables, Florida, 33146, United States
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University of Pennsylvania
Philadelphia, Pennsylvania, 19104, United States
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University of Rochester
Rochester, New York, 14642, United States
Conditions
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