Can a second treatment boost gene therapy for babies with SMA?
NCT ID NCT07444450
First seen Mar 20, 2026 · Last updated May 18, 2026 · Updated 4 times
Summary
This study tests a drug called salanersen in babies with spinal muscular atrophy (SMA) who already received gene therapy. The goal is to see if adding salanersen is safe and helps improve muscle function. About 42 infants with two copies of the SMN2 gene will take part. The study is double-blind and lasts up to 5.5 years.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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