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Breakthrough trial tests immune treatment for mysterious childhood brain disorder

NCT ID NCT04508530

Summary

This Phase 3 study tested whether Panzyga (an intravenous immunoglobulin treatment) works better than a placebo for children with Pediatric Acute-onset Neuropsychiatric Syndrome (PANS/PANDAS). The trial involved 71 children and teenagers aged 6-17 who suddenly developed severe obsessive-compulsive behaviors and other neuropsychiatric symptoms. Researchers measured changes in symptoms over 9 weeks to see if the immune-based treatment provided meaningful relief.

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Contacts and locations

Locations

  • Octapharma Research Site

    Tucson, Arizona, 85712, United States

  • Octapharma Research Site

    Little Rock, Arkansas, 72202, United States

  • Octapharma Research Site

    Los Angeles, California, 90024, United States

  • Octapharma Research Site

    Palo Alto, California, 94305, United States

  • Octapharma Research Site

    Centennial, Colorado, 80112, United States

  • Octapharma Research Site

    Boston, Massachusetts, 02114, United States

  • Octapharma Research Site

    Lebanon, New Hampshire, 03756, United States

  • Octapharma Research Site

    Genova, 16147, Italy

  • Octapharma Research Site

    Roma, 00161, Italy

  • Octapharma Research Site

    Roma, 00186, Italy

  • Octapharma Research Site

    Gothenburg, 41685, Sweden

  • Octapharma Research Site

    Stockholm, 17164, Sweden

Conditions

Explore the condition pages connected to this study.