Gene therapy injection aims to halt rare blindness
NCT ID NCT07185256
First seen Nov 01, 2025 · Last updated May 21, 2026 · Updated 30 times
Summary
This early-stage trial tests a gene therapy called OPGx-BEST1 in 10 adults with two rare inherited eye diseases (BVMD and ARB) that cause vision loss. The treatment is injected under the retina in one eye to see if it is safe and can slow or stop disease progression. Participants will be followed for 5 years to monitor side effects and any vision changes.
Disclaimer
Read more
Show less
This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for ARB are added.
Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
Genom att skicka in godkänner du våra Användarvillkor
Study contacts
-
Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
-
Children's Hospital Los Angeles
RECRUITINGLos Angeles, California, 90027, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
Cincinnati Eye Institute
RECRUITINGCincinnati, Ohio, 45242, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
-
Retina Foundation of the Southwest
RECRUITINGDallas, Texas, 75231, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
-
Vitreo Retinal Associates
NOT_YET_RECRUITINGGainesville, Florida, 34481, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
Explore the condition pages connected to this study.