New hope for fabry patients with kidney failure?
NCT ID NCT04020055
First seen Oct 31, 2025 · Last updated Jun 18, 2026 · Updated 26 times
Summary
This study looks at how safe the drug migalastat is and how it works in the body for people with Fabry disease who also have severe kidney issues or are on dialysis. It involves 14 adults with a specific genetic type of Fabry disease. The goal is to understand how the drug behaves in these patients to help guide future treatment.
Disclaimer
Read more
Show less
This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for FABRY DISEASE are added.
Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
Genom att skicka in godkänner du våra Användarvillkor
Locations
-
Centro Hospitalar e Universitário de Coimbra (CHUC)
Coimbra, 3041-801, Portugal
-
Emory University
Atlanta, Georgia, 30322, United States
-
Hospital General Universitario Gregorio Marañon
Madrid, 28007, Spain
-
Hospital General Universitario de Elda
Elda, 03600, Spain
-
Hospital Universitari(o) de Bellvitge (HUB) Feixa Llarga
Barcelona, 08907, Spain
-
Lysosomal and Rare Disorders Research and Treatment Center, Inc
Fairfax, Virginia, 22030, United States
-
Osaka University Hospital
Suita, Osaka, 565-0871, Japan
-
Royal Melbourne Hospital
Parkville, Victoria, 3050, Australia
-
Royal Perth Hospital
Perth, Washington, 6000, Australia
-
Salford Royal Hospital
Salford, England, M6 8HD, United Kingdom
-
Shizuoka General Hospital
Shizuoka, Shizuoka, 420-8527, Japan
-
The Cleveland Clinic
Cleveland, Ohio, 44195, United States
Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.