Gene therapy for inherited deafness: long-term safety check begins
NCT ID NCT06696456
First seen Mar 11, 2026 · Last updated May 22, 2026 · Updated 6 times
Summary
This study checks the long-term safety and effectiveness of a gene therapy called AAVAnc80-hOTOF in 30 people with hearing loss due to otoferlin gene mutations. All participants previously received the therapy in an earlier trial. Researchers will watch for late side effects and measure hearing changes over time.
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This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
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Locations
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Boston Children's Hospital
Boston, Massachusetts, 02115, United States
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Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, 19146, United States
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Hospital Sant Joan de Déu
Esplugues de Llobregat, Barcelona, 08950, Spain
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National Taiwan University Hospital
Taipei, Taiwan, (R.O.C), 100, Taiwan
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University of Iowa
Iowa City, Iowa, 52242, United States
Conditions
Explore the condition pages connected to this study.