Gene therapy recipients monitored for years ahead
NCT ID NCT05506254
First seen Nov 01, 2025 · Last updated May 20, 2026 · Updated 30 times
Summary
This study follows 4 patients with methylmalonic acidemia (MMA) who previously received the experimental gene therapy hLB-001. Researchers are tracking any long-term side effects or health problems that may appear over time. The goal is to understand the lasting safety of this treatment, not to test a new therapy.
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This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Clinical Trial Site
Atlanta, Georgia, 30322, United States
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Clinical Trial Site
Pittsburgh, Pennsylvania, 15224, United States
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Clinical Trial Site
Nashville, Tennessee, 37232, United States
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Clinical Trial Site
Seattle, Washington, 98105, United States
Conditions
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