Gene therapy breakthrough aims to stop sickle cell pain
NCT ID NCT07436767
First seen Feb 28, 2026 · Last updated May 23, 2026 · Updated 10 times
Summary
This study tests a new treatment called KL003 for people with severe sickle cell disease. The treatment uses a patient's own blood stem cells, modified with a healthy gene, to help produce normal red blood cells. Three participants aged 12 to 50 will receive a single infusion. The goal is to see if the treatment safely reduces painful episodes and improves blood counts.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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