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New oral drug could transform life for PKU patients

NCT ID NCT06971731

Summary

This study is testing whether an oral medication called JNT-517 can safely lower harmful phenylalanine levels in adults with PKU. About 120 participants will take either the drug or a placebo twice daily for up to a year while maintaining their special diet. Researchers will measure how well the drug controls phenylalanine levels and monitor for side effects throughout the 400-day study.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Ann & Robert H. Lurie Children's Hospital of Chicago

    RECRUITING

    Chicago, Illinois, 60611, United States

    Contact

  • Beatrix Children's Hospital

    RECRUITING

    Groningen, Netherlands

    Contact

  • Centre Hospitalier Régional Universitaire (CHRU) de Tours - Hôpital Bretonneau

    RECRUITING

    Tours, France

    Contact

  • Fakultní nemocnice Královské Vinohrady

    RECRUITING

    Prague, Czechia

    Contact

  • Fujita Health University

    RECRUITING

    Kutsukake-cho, Japan

    Contact

  • Hospital Clinico Universitario de Santiago de Compostela

    RECRUITING

    Santiago de Compostela, Spain

    Contact

  • Hospital Universitario Ramón y Cajal

    RECRUITING

    Madrid, Spain

    Contact

  • M.A.G.I.C Clinic

    RECRUITING

    Calgary, Alberta, T2E 7H7, Canada

    Contact

  • Mater Health - Mater Hospital Brisbane

    RECRUITING

    South Brisbane, 4104, Australia

    Contact

  • Nihon University Hospital

    RECRUITING

    Chiyoda-ku, Japan

    Contact

  • Oregon Health and Science University

    RECRUITING

    Portland, Oregon, 97239, United States

    Contact

  • Osaka Metropolitan University Hospital

    RECRUITING

    Osaka, Japan

    Contact

  • Pomorski Uniwersytet Medyczny w Szczecinie

    RECRUITING

    Szczecin, Poland

    Contact

  • Royal Adelaide Hospital

    RECRUITING

    Adelaide, 5000, Australia

    Contact

  • Royal Melbourne Hospital

    RECRUITING

    Parkville, Australia

    Contact

  • Universitair Medisch Centra (AMC)- Amsterdam

    RECRUITING

    Amsterdam, Netherlands

    Contact

  • University of California Los Angeles (UCLA) School of Medicine

    RECRUITING

    Los Angeles, California, 90024, United States

    Contact

  • University of Florida (UF) Health Shands Hospital

    RECRUITING

    Gainesville, Florida, 32608, United States

    Contact

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh

    RECRUITING

    Pittsburgh, Pennsylvania, 15201, United States

    Contact

  • University of Texas Health (UTHealth) Science Center at Houston

    RECRUITING

    Houston, Texas, 77030-1501, United States

    Contact

  • University of Texas Southwestern

    RECRUITING

    Dallas, Texas, 75390, United States

    Contact

  • Universitätsklinikum Münster

    RECRUITING

    Münster, Germany

    Contact

  • Utah Health - The University of Utah Hospital

    RECRUITING

    Salt Lake City, Utah, 84112, United States

    Contact

  • Vanderbilt University Medical Center

    RECRUITING

    Nashville, Tennessee, 37232, United States

    Contact

Conditions

Explore the condition pages connected to this study.