New drug trial aims to slow rare nerve disease progression
NCT ID NCT07191912
Summary
This study is testing whether a daily oral drug called govorestat can provide long-term benefits for people with a specific genetic form of Charcot-Marie-Tooth disease (CMT-SORD). About 155 patients aged 16-65 will take either the drug or a placebo for up to three years to see if it improves walking, strength, and daily function. The goal is to control the disease by lowering toxic sorbitol levels in the blood, which are thought to damage nerves.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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CHU La Timone
Marseille, 13005, France
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Carlo Besta Neurological Institute
Milan, 20133, Italy
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Charité - Universitätsmedizin Berlin
Berlin, 10117, Germany
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Clinic for Special Children
Gordonville, Pennsylvania, 17529, United States
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Institut de Myologie
Paris, 75013, France
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Istanbul University
Istanbul, 34093, Turkey (Türkiye)
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Koç University Hospital
Istanbul, 34010, Turkey (Türkiye)
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La Fe University and Polytechnic Hospital
Valencia, 46026, Spain
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Sydney Childrens
Sydney, 2013, Australia
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Uniklinik of the RWTH Aachen University
Aachen, 52074, Germany
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University Medicine Gottingen (UMG)
Göttingen, 37075, Germany
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University of Iowa
Iowa City, Iowa, 52242, United States
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Vall d'Hebron Institut de Recerca (VHIR)
Barcelona, 08035, Spain
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Conditions
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