Single gene therapy injection tested to halt blindness
NCT ID NCT02652767
Summary
This study tested whether a single injection of an experimental gene therapy, called GS010, could improve vision in people with a rare inherited eye disease called Leber Hereditary Optic Neuropathy (LHON). The trial involved 39 participants who had recently started losing their vision (within the last 6 months). Researchers compared the effects of the real injection to a sham (placebo) procedure to see if the therapy was effective.
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Contacts and locations
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Locations
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Centre National Hospitalier d'Ophtalmologie des Quinze-VingtCentre National Hospitalier d'Ophtalmologie des Quinze-Vingt
Paris, Paris, France
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Department of Neurology, University of Munich, Friedrich-Baur-Institute
Munich, 80336, Germany
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Department of Ophthalmology, Emory University School of Medicine
Atlanta, Georgia, 30322, United States
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Doheny Eye Center, University of California, Los Angeles
Los Angeles, California, 91105, United States
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IRCCS Istituto delle Scienze Neurologiche di Bologna, UOC Clinica Neurologica, Ospedale Bellaria
Bologna, Bologna, Italy
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Moorfields Eye Hospital NHS Foundation Trust
London, EC1V 2PD, United Kingdom
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Neuro Ophthalmologic Associates, Wills Eye Hospital, Thomas Jefferson University
Philadelphia, Pennsylvania, 19107, United States
Conditions
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