One-Shot gene therapy aims to free patients from frequent bleeding treatments
NCT ID NCT05203679
Summary
This study is testing a single injection of an experimental gene therapy called BBM-H901 for adults with severe Hemophilia B. The goal is to see if the therapy is safe and if it can help the body produce its own missing clotting factor, which could reduce or eliminate the need for regular factor IX infusions. Researchers will monitor participants for a year to check for side effects and measure changes in bleeding rates and factor levels.
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Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
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Locations
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Anhui Provincial Hospital
Hefei, Anhui, 230022, China
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Henan Cancer Hospital
Zhengzhou, Henan, 450003, China
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Institute of Hematology & Blood Diseases Hospital Chinese Academy of Medical Sciences & Peking Union Medical College
Tianjin, Tianjin Municipality, 300020, China
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Nanfang Hospital Southern Medical University
Guangzhou, Guangdong, 510515, China
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North China University of Science and Technology Affiliated Hospital
Tangshan, Hebei, 063000, China
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Peking Union Medical College Hospital
Beijing, Beijing Municipality, 100005, China
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The Second Hospital of Shanxi Medical University
Taiyuan, Shanxi, 030001, China
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The Second People's Hospital of Shenzhen
Shenzhen, Guangdong, 518025, China
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The second Affiliated Hospital of Kunming Medical University
Kunming, Yunnan, 650032, China
Conditions
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