Lifeline for duchenne boys: expanded access to experimental steroid alternative
NCT ID NCT03863119
First seen Oct 31, 2025 · Last updated May 23, 2026 · Updated 23 times
Summary
This program offers continued treatment with vamorolone, a potential steroid alternative, to boys with Duchenne muscular dystrophy who finished earlier studies. It aims to keep them on the drug while the company prepares its FDA application. Participants must have completed specific prior studies at U.S. or Canadian sites and agree to follow the treatment plan.
Disclaimer
Read more
Show less
This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for DUCHENNE MUSCULAR DYSTROPHY are added.
Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
Genom att skicka in godkänner du våra Användarvillkor
Study contacts
-
Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
-
Alberta's Children Hospital
AVAILABLECalgary, Alberta, T3B 6A8, Canada
Contact
Contact Phone: •••-•••-••••
-
British Columbia Children's Hospital
AVAILABLEVancouver, British Columbia, V6H 3N1, Canada
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Email: •••••@•••••
-
Children's Hospital of Eastern Ontario
AVAILABLEOttawa, Ontario, K1H 8L1, Canada
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
Duke University
AVAILABLEDurham, North Carolina, 27710, United States
Contact
-
Montreal Childrens Hospital
AVAILABLEMontreal, Quebec, H4A 3J1, Canada
Contact Email: •••••@•••••
Contact
-
Nemours Children's Hospital
AVAILABLEOrlando, Florida, 32827, United States
Contact
-
Schneider Chidlren's Medical Center
AVAILABLEPetah Tikva, 4920435, Israel
Contact
-
Seattle Children's
AVAILABLESeattle, Washington, 98105, United States
Contact
-
The Hospital for Sick Children
AVAILABLEToronto, Ontario, M5G 1X8, Canada
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
-
University of California Davis
AVAILABLEDavis, California, 95616, United States
Contact
-
University of Texas Southwestern Medical Center
AVAILABLEDallas, Texas, 75207, United States
Contact
-
urie Children's Hospital of Chicago
AVAILABLEChicago, Illinois, 60611, United States
Contact
Conditions
Explore the condition pages connected to this study.