Gene therapy tested in single patient with rare blindness condition
NCT ID NCT03672968
First seen Mar 10, 2026 · Last updated May 25, 2026 · Updated 10 times
Summary
This expanded access program allowed one patient with Leber Hereditary Optic Neuropathy (a genetic condition causing vision loss) to receive GS010 gene therapy via injections into both eyes. The goal was to assess safety, not to cure the disease. The study is no longer available.
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This is a summary of
the original study
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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