Last hope: experimental drug tested in single patient with rare fatal brain disorder
NCT ID NCT07272525
First seen Jan 04, 2026 · Last updated May 19, 2026 · Updated 22 times
Summary
This study provides an experimental drug called fosigotifator to one patient with Cree Leukoencephalopathy, a rare and fatal brain disease that currently has no treatments. The drug aims to slow or stop brain damage and improve quality of life. The patient must be in early stages of the disease.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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McGill University Health Centre
Montreal, Quebec, H4A3J1, Canada
Conditions
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