Gene-Edited cells could reduce bleeding in severe hemophilia b
NCT ID NCT06611436
First seen Nov 01, 2025 · Last updated May 16, 2026 · Updated 29 times
Summary
This study tests a single infusion of BE-101, made from a person's own blood cells that are gene-edited to produce clotting factor IX. It aims to safely raise factor levels and reduce bleeding episodes in 24 adults with moderately severe to severe hemophilia B. Participants must currently use preventive factor treatment and have adequate organ function.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Email: •••••@•••••
Locations
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University of California, Davis
RECRUITINGDavis, California, 95616, United States
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University of Michigan
RECRUITINGAnn Arbor, Michigan, 48109, United States
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University of Minnesota
RECRUITINGMinneapolis, Minnesota, 55455, United States
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Washington Center for Bleeding Disorders
RECRUITINGSeattle, Washington, 98101, United States
Conditions
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