One-time gene infusion aims to strengthen failing hearts in rare genetic disease
NCT ID NCT07137338
First seen Feb 03, 2026 · Last updated May 24, 2026 · Updated 17 times
Summary
This early-stage trial tests a single intravenous dose of a gene therapy (RP-A701) in 8 adults with dilated cardiomyopathy caused by BAG3 gene mutations. The goal is to see if the treatment is safe and can improve heart function. Participants must be 18-65 years old with mild to moderate heart weakness.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Mayo Clinic
RECRUITINGRochester, Minnesota, 55905, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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Medical University of South Carolina
RECRUITINGCharleston, South Carolina, 29425, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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University of California, San Diego
RECRUITINGSan Diego, California, 92037, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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