Scientists track rare disease for clues to better care
NCT ID NCT03204370
Summary
This study aimed to learn more about the long-term progression of a rare, milder form of Morquio A disease in adults. Researchers followed 9 patients over 5 years to see how their symptoms changed, whether they were on treatment or not. The goal was to gather detailed information to help doctors better monitor the disease and evaluate treatments in the future.
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Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
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Genom att skicka in godkänner du våra Användarvillkor
Locations
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Rheumatology department - Bordeaux University Hospital
Bordeaux, Aquitaine, 33076, France
Conditions
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