New hope for FSHD: experimental drug AOC 1020 tested in humans
NCT ID NCT05747924
First seen Apr 29, 2026 · Last updated May 01, 2026 · Updated 1 time
Summary
This study tested an experimental drug called AOC 1020 in 90 adults with facioscapulohumeral muscular dystrophy (FSHD), a rare genetic disease that causes progressive muscle weakness. The main goals were to check the drug's safety and how the body processes it. Participants received either the drug or a placebo by IV, and researchers also looked for early signs that the drug might help control the disease.
Disclaimer
Read more
Show less
This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for FSHD2 are added.
Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
Genom att skicka in godkänner du våra Användarvillkor
Locations
-
Duke University
Durham, North Carolina, 27708, United States
-
Kansas University Medical Center
Kansas City, Kansas, 66205, United States
-
Ohio State University
Columbus, Ohio, 43221, United States
-
Rare Disease Research
Atlanta, Georgia, 30329, United States
-
Stanford University
Palo Alto, California, 94304, United States
-
University College London
London, WIT 7HA, United Kingdom
-
University of California Los Angeles
Los Angeles, California, 90095, United States
-
University of California San Diego
San Diego, California, 92093, United States
-
University of Colorado
Denver, Colorado, 80045, United States
-
University of Florida
Gainesville, Florida, 32608, United States
-
University of Ottawa
Ottawa, Ontario, K1Y 4E9, Canada
-
University of Pennsylvania
Philadelphia, Pennsylvania, 19104, United States
-
University of Rochester Medical Center
Rochester, New York, 14642, United States
-
University of Sheffield
Sheffield, S10 2TN, United Kingdom
-
University of Texas Southwestern
Dallas, Texas, 75390, United States
-
University of Washington
Seattle, Washington, 98104, United States
-
Virginia Commonwealth University
Richmond, Virginia, 23298, United States
Conditions
Explore the condition pages connected to this study.