Steroid-refractory Diamond-Blackfan anemia (DBA)

Clinical trials for Steroid-refractory Diamond-Blackfan anemia (DBA) explained in plain language.

Never miss a new study

Get alerted when new Steroid-refractory Diamond-Blackfan anemia (DBA) trials appear

Sign up with your email to follow new studies for Steroid-refractory Diamond-Blackfan anemia (DBA), keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.

Vår säkerhetsrekommendation!

Genom att skicka in godkänner du våra Användarvillkor

Completed 1

New hope for rare blood disorder: experimental pill reduces need for transfusions

Disease control Completed

This study tested a drug called bitopertin in 15 adults with Diamond-Blackfan anemia (DBA), a rare inherited condition that causes severe anemia. Participants took the pill daily for 8 months, with doses possibly increasing over time. The goal was to see if the drug could raise h…

Matched conditions: STEROID-REFRACTORY DIAMOND-BLACKFAN ANEMIA (DBA)

Phase 1/2 • Sponsor: National Heart, Lung, and Blood Institute (NHLBI) • Aim: Disease control

Last updated Jul 02, 2026 00:00 UTC

Steroid-refractory Diamond-Blackfan anemia (DBA)

Get alerted when new Steroid-refractory Diamond-Blackfan anemia (DBA) trials appear

New hope for rare blood disorder: experimental pill reduces need for transfusions