Muscular dystrophy, Duchenne
Clinical trials for Muscular dystrophy, Duchenne explained in plain language.
Never miss a new study
Get alerted when new Muscular dystrophy, Duchenne trials appear
Sign up with your email to follow new studies for Muscular dystrophy, Duchenne, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
Genom att skicka in godkänner du våra Användarvillkor
-
New gene therapy trial hopes to restore muscle protein in duchenne boys
Disease control Recruiting nowThis study tests a one-time gene therapy called delandistrogene moxeparvovec in 83 people with Duchenne muscular dystrophy. The goal is to see if it is safe and helps the body make dystrophin, a protein missing in Duchenne. The trial is now enrolling non-ambulatory participants (…
Matched conditions: MUSCULAR DYSTROPHY, DUCHENNE
Phase 1 • Sponsor: Sarepta Therapeutics, Inc. • Aim: Disease control
Last updated Sep 13, 2026 00:00 UTC
-
New hope for duchenne: targeted therapy now available for eligible patients
Disease control Expanded accessThis program provides access to an experimental drug, AOC 1044, for people with Duchenne muscular dystrophy (DMD) whose genetic mutation can be treated by skipping exon 44. The goal is to help control the disease and improve muscle function. Participants must be at least 2 years …
Matched conditions: MUSCULAR DYSTROPHY, DUCHENNE
Sponsor: Avidity Biosciences, Inc. • Aim: Disease control
Last updated Sep 03, 2026 00:00 UTC
-
New drug could help boys with duchenne walk and move longer
Disease control Recruiting nowThis study tests a new medicine called DYNE-251 in boys aged 4 to 18 with Duchenne muscular dystrophy (DMD) who can still walk. The goal is to see if it helps them move better and slows muscle damage. Participants will receive either the drug or a placebo every 4 weeks for about …
Matched conditions: MUSCULAR DYSTROPHY, DUCHENNE
Phase 3 • Sponsor: Dyne Therapeutics • Aim: Disease control
Last updated Jun 27, 2026 12:37 UTC
-
Blood test could replace risky needle for prenatal genetic diagnosis
Diagnosis Recruiting nowThis study is testing a new blood test that can diagnose single-gene disorders in unborn babies using a sample from the mother. The test looks at fetal DNA found in the mother's blood, which is safer than traditional invasive methods that carry a small risk of miscarriage. Resear…
Matched conditions: MUSCULAR DYSTROPHY, DUCHENNE
Sponsor: Assistance Publique - Hôpitaux de Paris • Aim: Diagnosis
Last updated Jun 27, 2026 12:23 UTC