MUSCULAR DYSTROPHY, DUCHENNE
Clinical trials for MUSCULAR DYSTROPHY, DUCHENNE explained in plain language.
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Gene therapy trial hopes to restore muscle protein in duchenne patients
Disease control Recruiting nowThis study tests a gene therapy called delandistrogene moxeparvovec (SRP-9001) in people with Duchenne muscular dystrophy (DMD). The goal is to see if it is safe and can help the body produce dystrophin, a protein missing in DMD. The trial includes children and adults, both able …
Matched conditions: MUSCULAR DYSTROPHY, DUCHENNE
Phase: PHASE1 • Sponsor: Sarepta Therapeutics, Inc. • Aim: Disease control
Last updated May 26, 2026 05:37 UTC
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New hope for DMD: experimental drug opens to more patients
Disease control AVAILABLEThis program provides access to an investigational drug, AOC 1044, for people with Duchenne muscular dystrophy (DMD) whose genetic mutation can be treated by skipping exon 44. It is for eligible patients aged 6 and older living in the US. The goal is to offer treatment while gath…
Matched conditions: MUSCULAR DYSTROPHY, DUCHENNE
Sponsor: Avidity Biosciences, Inc. • Aim: Disease control
Last updated May 26, 2026 04:36 UTC
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New blood test could replace risky prenatal procedures for genetic diseases
Diagnosis Recruiting nowThis study is testing a blood test that can check for genetic disorders in unborn babies without the risks of traditional invasive tests. The test looks at fetal DNA found in the mother's blood as early as 9 weeks into pregnancy. Researchers aim to make this safe, accurate diagno…
Matched conditions: MUSCULAR DYSTROPHY, DUCHENNE
Sponsor: Assistance Publique - Hôpitaux de Paris • Aim: Diagnosis
Last updated May 26, 2026 05:27 UTC
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Fabric brace may give weak arms a lift
Symptom relief Recruiting nowThis study tests a special fabric shoulder brace designed to mimic muscle action. Researchers want to see if it helps people with neuromuscular disorders (like muscular dystrophy or ALS) move their arms and hands better. About 30 participants will be evaluated with and without th…
Matched conditions: MUSCULAR DYSTROPHY, DUCHENNE
Phase: NA • Sponsor: Seoul National University Hospital • Aim: Symptom relief
Last updated May 26, 2026 05:31 UTC