Gaucher's disease type I

Clinical trials for Gaucher's disease type I explained in plain language.

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Completed 1

New oral drug shows promise for kids with gaucher disease

Disease control Completed

This study tested the safety and effectiveness of eliglustat, an oral medication, in 57 children aged 2 to 17 with Gaucher disease types 1 and 3. Some children also received the standard enzyme therapy imiglucerase. Researchers measured how the drug moves through the body, side e…

Matched conditions: GAUCHER'S DISEASE TYPE I

Phase 3 • Sponsor: Sanofi • Aim: Disease control

Last updated Jun 27, 2026 14:00 UTC

Gaucher's disease type I

Get alerted when new Gaucher's disease type I trials appear

New oral drug shows promise for kids with gaucher disease