EXTRAVASCULAR HEMOLYSIS
Clinical trials for EXTRAVASCULAR HEMOLYSIS explained in plain language.
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New hope for PNH patients: early access to danicopan for hard-to-treat anemia
Disease control AVAILABLEThis program provides early access to danicopan for adults with paroxysmal nocturnal hemoglobinuria (PNH) who have significant extravascular hemolysis (EVH) despite current treatment with Soliris or Ultomiris. Participants must be at least 18 years old, have anemia and high retic…
Matched conditions: EXTRAVASCULAR HEMOLYSIS
Sponsor: Alexion Pharmaceuticals, Inc. • Aim: Disease control
Last updated May 22, 2026 13:50 UTC
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New hope for kids with rare blood disease: Add-On pill may boost red blood cells
Disease control Recruiting nowThis study tests whether adding danicopan (a pill) to standard PNH therapy (ravulizumab or eculizumab) can improve hemoglobin levels in children aged 12 to 17 with paroxysmal nocturnal hemoglobinuria (PNH) who still have anemia due to extravascular hemolysis. About 6 participants…
Matched conditions: EXTRAVASCULAR HEMOLYSIS
Phase: PHASE3 • Sponsor: Alexion Pharmaceuticals, Inc. • Aim: Disease control
Last updated May 18, 2026 12:12 UTC