ADENOSINE DEAMINASE SEVERE COMBINED IMMUNE DEFICIENCY

Clinical trials for ADENOSINE DEAMINASE SEVERE COMBINED IMMUNE DEFICIENCY explained in plain language.

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Bubble boy disease gene therapy shows promise in new trial

Disease control Recruiting now

This study tests a gene therapy for children with ADA-SCID, a severe immune disorder often called 'bubble boy disease.' The treatment uses the child's own blood stem cells, which are modified in a lab to correct the genetic defect and then returned to the body. The goal is to res…

Matched conditions: ADENOSINE DEAMINASE SEVERE COMBINED IMMUNE DEFICIENCY

Phase: PHASE1, PHASE2 • Sponsor: University of California, Los Angeles • Aim: Disease control

Last updated May 26, 2026 03:12 UTC

ADENOSINE DEAMINASE SEVERE COMBINED IMMUNE DEFICIENCY

Get alerted when new ADENOSINE DEAMINASE SEVERE COMBINED IMMUNE DEFICIENCY trials appear

Bubble boy disease gene therapy shows promise in new trial