Diamond-Blackfan anemia
MONDO:0015253A congenital aregenerative and often macrocytic anemia with erythroblastopenia.
Also known as: Aase syndrome, Aase-Smith II syndrome, Blackfan-Diamond anaemia, Blackfan-Diamond anemia, DBA, Diamond Blackfan Anemia, Diamond-Blackfan anemia, chronic constitutional pure red cell anemia
26 clinical trials for this condition and its sub-types, 17 tagged with Diamond-Blackfan anemia itself.
Follow this condition to get notified about new trialsWhere it sits in the disease tree
Browse by category →Sub-types of Diamond-Blackfan anemia
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Diamond-Blackfan anemia 1 1 trial
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Diamond-Blackfan anemia 10 0 trials
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Diamond-Blackfan anemia 11 0 trials
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Diamond-Blackfan anemia 12 0 trials
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Diamond-Blackfan anemia 13 0 trials
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Diamond-Blackfan anemia 16 0 trials
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Diamond-Blackfan anemia 17 0 trials
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Diamond-Blackfan anemia 18 0 trials
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Diamond-Blackfan anemia 19 0 trials
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Diamond-Blackfan anemia 2 0 trials
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Diamond-Blackfan anemia 20 0 trials
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Diamond-Blackfan anemia 21 0 trials
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Diamond-Blackfan anemia 22 0 trials
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Diamond-Blackfan anemia 3 0 trials
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Diamond-Blackfan anemia 4 0 trials
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Diamond-Blackfan anemia 5 0 trials
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Diamond-Blackfan anemia 6 0 trials
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Diamond-Blackfan anemia 7 0 trials
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Diamond-Blackfan anemia 8 0 trials
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Diamond-Blackfan anemia 9 0 trials
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New drug combo aims to make bone marrow transplants safer for kids
Disease control OngoingThis pilot study tests a fludarabine-based drug regimen to prepare children with bone marrow failure syndromes for a bone marrow transplant from a matched sibling donor. The goal is to help the donor cells successfully take root while reducing serious side effects. The study incl…
Early phase 1 • Sponsor: Children's Hospital of Philadelphia • Aim: Disease control
Last updated Jun 27, 2026 12:39 UTC
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New algorithm aims to catch ovarian damage early in young cancer survivors
Knowledge-focused CancelledThis study was designed to see if a new monitoring algorithm could detect early signs of ovarian damage in women and girls who had cancer treatment. Researchers planned to compare a group using the new algorithm with a group that received standard care. However, the study was wit…
Sponsor: University of Colorado, Denver • Aim: Knowledge-focused
Last updated Jun 26, 2026 17:42 UTC