Beta-thalassemia HBB/LCRB
MONDO:0013517Abnormal clinical manifestations of beta thalassemia that are as a result of the underlying genotype.
Also known as: thalassemia, beta, thalassemia, hispanic gamma-delta-beta, beta-thalassemia
81 clinical trials for this condition and its sub-types, 2 tagged with Beta-thalassemia HBB/LCRB itself.
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Sub-types of Beta-thalassemia HBB/LCRB
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Beta-thalassemia major 49 trials
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Beta-thalassemia intermedia 9 trials
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Thalassemia minor 1 trial
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Gene therapy aims to free patients from lifelong blood transfusions
Cure Recruiting nowThis study follows people who have already received an experimental gene therapy called BRL-101 for transfusion-dependent β-thalassemia, a severe blood disorder requiring regular transfusions. Researchers will monitor participants over the long term to check for safety issues, su…
Sponsor: Bioray Laboratories • Aim: Cure
Last updated Jul 23, 2026 00:00 UTC
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New transplant approach could help more patients with blood disorders
Disease control Recruiting nowThis study is testing a stem cell transplant from half-matched (haploidentical) donors for people with sickle cell disease or beta-thalassemia. Before the transplant, patients receive drugs to lower their immune system, which may reduce the risk of serious side effects like graft…
Phase 2 • Sponsor: Memorial Sloan Kettering Cancer Center • Aim: Disease control
Last updated Jun 27, 2026 13:00 UTC