Hope for rare eye disease: experimental gene therapy offered to control group

NCT ID NCT07307469

First seen Jan 07, 2026 · Last updated Apr 28, 2026 · Updated 16 times

Summary

This study provides the ZVS101e injection to 32 people with Bietti crystalline corneoretinal dystrophy who were previously in a control group. The goal is to offer treatment and check for side effects. Participants must have completed a 52-week follow-up in an earlier phase 3 trial.

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Contacts and locations

Locations

  • Henan Provincial People's Hospital

    Zhengzhou, Henan, China

  • Peking University Third Hospital

    Beijing, Beijing Municipality, China

  • Tianjin Medical University Eye Hospital

    Tianjin, Tianjin Municipality, China

  • West China Hospital, Sichuan University

    Chengdu, Sichuan, China

  • Zhongshan Ophthalmic Center, Sun Yat-sen University

    Guangzhou, Guangdong, China

Conditions

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