Promising drug for kids with rare muscle disease moves to next phase
NCT ID NCT06055959
First seen Jun 27, 2026 · Last updated Jul 31, 2026 · Updated 4 times
Summary
This study is testing a drug called zilucoplan in children aged 2 to 17 with generalized myasthenia gravis, a disease that causes muscle weakness. The goal is to see how the drug works in the body, if it is safe, and if it helps control the disease. Only 8 children will take part, and they will receive the drug without a placebo.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
Locations
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Mg0014 20104
WITHDRAWNSeoul, South Korea
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Mg0014 20220
RECRUITINGSeoul, South Korea
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Mg0014 40144
RECRUITINGMilan, Italy
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Mg0014 40218
ACTIVE_NOT_RECRUITINGWarsaw, Poland
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Mg0014 40735
RECRUITINGGlasgow, United Kingdom
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Mg0014 40736
RECRUITINGLondon, United Kingdom
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Mg0014 40774
RECRUITINGKatowice, Poland
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Mg0014 50168
WITHDRAWNChicago, Illinois, 60611, United States
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Mg0014 50574
WITHDRAWNFlower Mound, Texas, 75028, United States
More trials for these conditions
Other studies related to the condition(s) this trial covers.
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