New hope for kids with relapsed leukemia: targeted drug plus chemo enters trial

NCT ID NCT06376162

First seen Nov 01, 2025 · Last updated May 13, 2026 · Updated 26 times

Summary

This early-phase trial tests a new targeted drug called ziftomenib combined with chemotherapy in children and young adults (up to age 21) whose acute leukemia has returned or not responded to standard treatment. The study focuses on finding the safest dose and understanding how the drug works in the body. About 20 participants with specific genetic changes (KMT2A-r, NUP98-r, or NPM1-m) will be enrolled.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Ann & Robert H. Lurie Children's Hospital of Chicago

    RECRUITING

    Chicago, Illinois, 60611, United States

  • CHU de Nantes - Hôpital Femme-Enfant-Adolescent

    RECRUITING

    Nantes, Loire-Atlantique, 44093, France

  • CHU de Reims - Hôpital Robert Debré

    RECRUITING

    Paris, Île-de-France Region, 75019, France

  • Children's Healthcare of Atlanta

    RECRUITING

    Atlanta, Georgia, 30329, United States

  • Children's Hospital Colorado

    RECRUITING

    Aurora, Colorado, 80045, United States

  • Children's Hospital Los Angeles

    RECRUITING

    Los Angeles, California, 90027, United States

  • Children's Hospital of Philadelphia

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

  • Cincinnati Children's Hospital Medical Center

    RECRUITING

    Cincinnati, Ohio, 45229-3026, United States

  • Dana-Farber Cancer Institute

    RECRUITING

    Boston, Massachusetts, 02215, United States

  • Fondazione IRCCS San Gerardo dei Tintori (Ospedale San Gerardo)

    RECRUITING

    Monza, 20900, Italy

  • Hospital Infantil Universitario Niño Jesús

    RECRUITING

    Madrid, 28009, Spain

  • Hospital Universitari Vall d'Hebrón

    RECRUITING

    Barcelona, 08035, Spain

  • Memorial Sloan Kettering Cancer Center - New York

    RECRUITING

    New York, New York, 10065, United States

  • Ospedale Pediatrico Bambino Gesù

    RECRUITING

    Roma, Rome, 00165, Italy

  • Prinses Maxima Centrum Kinderoncologie

    RECRUITING

    Utrecht, 3584 CS, Netherlands

  • Sankt Anna-Kinderspital

    RECRUITING

    Vienna, State of Vienna, 1090, Austria

  • Seattle Children's Hospital

    RECRUITING

    Seattle, Washington, 98105, United States

  • SickKids - The Hospital for Sick Children

    RECRUITING

    Toronto, Ontario, M5G 1X8, Canada

  • St. Jude Children's Research Hospital

    RECRUITING

    Memphis, Tennessee, 38105-3678, United States

  • Texas Children's Hospital

    RECRUITING

    Houston, Texas, 77030, United States

Conditions

Explore the condition pages connected to this study.