New study tracks liver risks in rare muscle disease

NCT ID NCT06581146

First seen Nov 01, 2025 · Last updated May 13, 2026 · Updated 24 times

Summary

This study follows about 50 boys under 18 with XLMTM, a serious genetic muscle condition, for one year to see how often liver and gallbladder problems occur. Researchers will collect health information and use a special liver scan (Fibroscan) at home or in clinic. The goal is to better understand these issues and improve routine care for affected children.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for X-LINKED MYOTUBULAR MYOPATHY are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Ann & Robert H. Lurie Children's Hospital of Chicago

    RECRUITING

    Chicago, Illinois, 60611, United States

  • Boston Children's Hospital

    RECRUITING

    Boston, Massachusetts, 02115, United States

  • Children's Hospital of Philadelphia

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

  • Cincinnati Children's Hospital Medical Center

    RECRUITING

    Cincinnati, Ohio, 45229, United States

  • UPMC Children's Hospital of Pittsburgh

    RECRUITING

    Pittsburgh, Pennsylvania, 15224, United States

  • University of Utah

    RECRUITING

    Salt Lake City, Utah, 84112, United States

Conditions

Explore the condition pages connected to this study.