Scientists investigate genetic mysteries behind rare disease

NCT ID NCT07485413

Summary

This study aims to better understand how specific genetic changes affect Wolfram syndrome, a rare inherited disorder. Researchers are examining 45 participants who have genetic mutations associated with the condition, focusing on detailed eye scans. The goal is to determine which genetic changes actually cause disease symptoms versus those that may be harmless.

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Contacts and locations

Locations

  • HEGP

    Paris, 75015, France

Conditions

Explore the condition pages connected to this study.