New eye drug shows promise for rare Blindness-Causing mutation
NCT ID NCT05902962
First seen Apr 17, 2026 · Last updated May 21, 2026 · Updated 4 times
Summary
This early-stage study tested a new drug called VP-001, given as an injection into the eye, in 17 adults with a rare inherited retinal disease caused by a PRPF31 gene mutation. The main goal was to check if the treatment is safe and tolerable. The study did not aim to cure the disease, but to gather safety data for future research.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Bascom Palmer Eye Institute University of Miami
Miami, Florida, 33136, United States
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Baylor College of Medicine- Alkek Eye Center
Houston, Texas, 77030, United States
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Oregon Health and Science University - Casey Eye Institute
Portland, Oregon, 97239, United States
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Retina Foundation of the Southwest
Dallas, Texas, 75321, United States
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University of Florida Health
Jacksonville, Florida, 32209, United States
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University of Michigan Kellogg Eye Center
Ann Arbor, Michigan, 48105, United States
Conditions
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