Daily injection trial aims to help babies with dwarfism avoid risky spinal surgery
NCT ID NCT04554940
Summary
This study tests the safety of daily vosoritide injections in infants with achondroplasia (the most common form of dwarfism) who are at risk of needing spinal decompression surgery. Researchers want to see if the treatment is safe for very young children and whether it affects skull growth around the spinal cord. The trial includes 20 infants under 12 months old who show signs that might require surgery.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for ACHONDROPLASIA are added.
By submitting, you agree to our Terms of use
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
By submitting, you agree to our Terms of use
Locations
-
Guy's and St. Thomas NHS Foundation Trust Evelina Children's Hospital
London, SE1 7EH, United Kingdom
-
Murdoch Children's Research Institute
Parkville, Victoria, 3052, Australia
-
Sheffield Children's NHS Foundation Trust
Sheffield, S10 2TH, United Kingdom
Conditions
Explore the condition pages connected to this study.