New drug hopes to help kids with rare growth disorders grow taller

NCT ID NCT04219007

First seen Apr 28, 2026 · Last updated Apr 30, 2026 · Updated 1 time

Summary

This study tests a drug called vosoritide in 56 children with short stature caused by certain genetic conditions. The drug targets the growth plate to help children grow faster. Participants are observed for 6 months, then treated for 12 months with daily shots to see if it safely improves height and growth speed.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Children's National Hospital

    Washington D.C., District of Columbia, 20010, United States

Conditions

Explore the condition pages connected to this study.