New shot aims to stop bleeding in rare blood disorder

NCT ID NCT07115004

First seen Jun 26, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This phase 3 study tests a drug called VGA039, given as a shot under the skin, to prevent bleeding in people with Von Willebrand disease. The trial will include 60 patients aged 12 to 75 who have frequent bleeding episodes. Researchers will track how well the drug reduces bleeds and check for side effects over about a year.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

VGA039 (a drug given as a shot under the skin)

What this could lead to

If it works, this could offer a new preventive treatment to reduce bleeding episodes in people with Von Willebrand disease.

What could go wrong

This is still a phase 3 trial with only 60 participants, so results may not apply to everyone. There are risks like allergic reactions or side effects from the drug.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

von Willebrand disease (hereditary or acquired)

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Arkansas Children's Hospital

    RECRUITING

    Little Rock, Arkansas, 72202, United States

  • Charlotte Maxeke Johannesburg Academic Hospital School of Pathology Clinical Haematologist

    RECRUITING

    Johannesburg, 2194, South Africa

  • Children's Healthcare of Atlanta

    RECRUITING

    Atlanta, Georgia, 30329, United States

  • Emory University Hospital

    RECRUITING

    Atlanta, Georgia, 30308, United States

    Contact Phone: •••-•••-••••

  • Frankfurt University Hospital (Universitätsmedizin Frankfurt)

    RECRUITING

    Frankfurt, 60596, Germany

  • Hemophilia Center of Western PA

    RECRUITING

    Pittsburgh, Pennsylvania, 15213, United States

  • K Eristavi National Center of Experimental and Clinical Surgery (ქირურგიის ეროვნული ცენტრი)

    RECRUITING

    Tbilisi, 0159, Georgia

  • Luskin Orthopaedic Institute For Children

    RECRUITING

    Los Angeles, California, 90007, United States

  • Science 37, Inc. (Virtual Clinical MetaSite)

    RECRUITING

    Morrisville, North Carolina, 27560, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • UC Davis Medical Center

    RECRUITING

    Sacramento, California, 95817, United States

  • UT Southwestern Children's Hospital

    RECRUITING

    Dallas, Texas, 75235, United States

  • University of California San Francisco

    RECRUITING

    San Francisco, California, 94143, United States

  • University of Minnesota

    RECRUITING

    Minneapolis, Minnesota, 55455, United States

  • Washington Center for Bleeding Disorders

    RECRUITING

    Seattle, Washington, 98101, United States

    Contact Email: •••••@•••••