Cancer drug shows promise for rare blood vessel disorders in kids
NCT ID NCT07549646
First seen Apr 25, 2026 · Last updated May 10, 2026 · Updated 1 time
Summary
This study tests the drug trametinib, already approved for melanoma, in people aged 2 months to 30 years with rare blood vessel growth problems caused by a specific gene pathway. The goal is to see if the drug can shrink abnormal vessels and improve quality of life. Participants take the drug for 2-3 years and attend up to 16 clinic visits.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, 19104, United States
Conditions
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